Programme

The conference will take place at İstanbul Nişantaşı University in Istanbul, Turkey. The conference will start on Friday morning at 10:30 (March 27, 2026) and end on Sunday afternoon at 14:00 (March 29, 2026), after lunch.

There will be 5 sessions, interrupted by joint coffee breaks and lunches around the company booths, and dinner outside the venue (on Friday and Saturday) to enable interaction and fruitful collaborations among those involved in therapy development for LAMA2-RD.

In sessions 1-3, young scientists from clinics, universities, or companies will be encouraged to present their work, as they represent the future of LAMA2-RD research. Day 2 focuses on patients and their needs; session 4 will take place, and will have an open, informal character to stimulate engagement between the patients and their representatives, scientists, clinicians and company representatives. This will include international online involvement for those not able to be present on-site. Session 5 will address the regulatory paths needed to keep the costs of therapy development low to make it broadly accessible for the patients who need it. This will require a joint address of scientists, clinicians and patients toward regulatory authorities.

For the children, a playground will be organised, allowing them to have fun with patients from other countries.

Pre-conference lectures

For parents and family members

Day 1: March 27th

Morning

Session 1: Clinical manifestations and care

Afternoon

Session 2: Natural history and trial readiness

Afternoon and Evening

Session 3: The road to therapy

Day 2: March 28th

Morning and afternoon

Session 4: Patients and their needs

Day 3: March 29th

Session 5: Accelerating on the bumpy road to therapy

Morning